RARE DISEASE GENE THERAPY PRESS KIT
Gene Therapy: Imagine the Possibilities
More than 80% of rare diseases have a known genetic component. At Pfizer Rare Disease, we are exploring the potential of gene therapy to treat these rare genetic diseases through potentially life-changing innovations, trusted partnerships, and relentless passion. Through our research, it has become clear that genetics may not have to determine the future of a person living with a rare disease.
Gene therapy is a potentially transformative treatment approach that, if successful, may help reduce the burden of ongoing treatments for nearly 320 million people worldwide who are affected by rare genetic diseases. If we are successful, imagine the possibilities.
Learn more about our innovative approach to addressing rare genetic diseases:
GENE THERAPY: QUICK FACTS
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Gene Therapy: Pioneering A New Era of Care
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Gene Therapy: Frequently Asked Questions
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Pfizer Rare Disease has been and will continue to be a part of the journey with the rare disease community. We are here to listen, to learn, and to make a difference in the lives of those affected by rare diseases.
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